The Journal of the Arkansas Medical Society Med Journal Feb 2020_Final | Seite 18
setting with health care providers with expertise
in managing these patients. The 2007 consen-
sus guidelines and the update published as Part
1 and Part 2 in 2018 established the need for a
multidisciplinary approach to SMA care. Such
comprehensive care for patients with SMA may
best be achieved at a tertiary care center. 2,6
Ongoing research has shown that beginning ther-
apy as early as possible in children with SMA is
critical. Studies indicate therapy is most effective
when it can begin in the first few months of life
before significant motor neuron loss occurs as
well as in pre-symptomatic infants. This research
reinforces the need for newborn screening,
which would eliminate long and costly diagnos-
tic delays and allow pre-symptomatic therapy.
The CureSMA advocacy group lobbied the U.S.
Congress to include SMA in the Recommended
Uniformed Screening Panel for newborn screen-
ing. Several U.S. states initiated pilot programs
in 2018, and the testing has been shown to be
highly specific and sensitive. It is gratifying that in
Arkansas, Governor Asa Hutchinson has signed
a bill (HB 1074) into law that requires testing for
SMA be added to the state’s newborn screening
panel. This will allow for genetic diagnosis soon
For many
clinics, group
membership
in the
Arkansas
Medical
Society eliminates the hassle
of individual renewal and
reimbursement for physicians
and accounts payable staff and
provides EVERY physician with
the invaluable resources of the
largest and strongest Arkansas
health care advocate.
after birth, potentially even before onset of any
symptoms. 8,9,10
In conclusion, patients with SMA, a previously
incurable and debilitating disease, now have a
chance to greatly modify the condition and there-
by extend the length and improve the quality of
their lives.
References
1. Ogino S, Winson RB. Genetic testing and risk
assessment for spinal muscular atrophy (SMA).
Hum Genet. 2002 Dec;111(6):477-500.
2. Pechmann A, Kirschner J. Diagnosis and New
Treatment Avenues in Spinal Muscular Atrophy.
Neuropediatrics. 2017 Aug; 48(4): 273-281.
3. Veerapandiyan A, Ciafaloni E. Spinal muscu-
lar atrophy. MedLink Neurology. http://www.
medlink.com/article/spinal_muscular_atrophy.
4. Reed UC, Zanoteli E. Therapeutic advances in
5q-linked spinal muscular atrophy. Arq Neurop-
siquiatr. 2018 Apr;76(4):265-272.
5. Mesfin A, Sponseller PD, Leet AI. Spinal mus-
cular atrophy: manifestations and management. J
Am Acad Orthop Surg. 2012 Jun;20(6):393-401.
6. Michelson D, Ciafaloni E, Ashwal S et al. Ev-
idence in focus: Nusinersen use in spinal mus-
cular atrophy: Report of the Guideline Devel-
opment, Dissemination, and Implementation
Subcommittee of the American Academy of Neu-
rology. Neurology 2018 Nov 13; 91(20):923-933.
7. Mendell JR, Al-Zaidy S, Shell R et al. Sin-
gle-Dose Gene-Replacement Therapy for Spinal
Muscular Atrophy. N Engl J Med. 2017 Nov 2;
377(18): 1713-1722.
8. Lin CW, Kalb SJ, Yeh WS. Delay in Diagnosis
of Spinal Muscular Atrophy: A Systematic Liter-
ature Review. Pediatr Neurol. 2015 Oct; 53(4):
293-300.
9. Phan HC, Taylor JL, Hannon H, Howell R.
Newborn screening for spinal muscular atrophy:
Anticipating an imminent need. Semin Perinatol.
2015 Apr; 39(3): 217-29.
10. Glascock J, Sampson J, Haidet-Phillips A et
al. Treatment Algorithm for Infants Diagnosed
with Spinal Muscular Atrophy through Newborn
Screening. J Neuromuscul Dis. 2018; 5(2): 145-
158.
Thank
you
TO OUR 2020 AMS GROUP MEMBERS
We invite groups of 5 or more
physicians to take advantage of
the AMS Group Memberaship
Program. Our goal with this
program is to be able to provide
the practice management
resources your practice needs
and the advocacy that the
physician needs in one group
benefit.
166 • The Journal of the Arkansas Medical Society
Arkansas Asthma and Allergy Doctors’ Anatomic Pathology
St. Mary’s- Millard Henry
Arkansas Cardiology
Services, PA
Clinic
Arkansas Heart Hospital
GastroArkansas
Monticello Medical Clinic
Arkansas Methodist Medical
CHI St. Vincent Heart Clinic
Mercy Obstetrics and
Center
Arkansas
Gynecology
All for Kids Pedicatric Care
Highlands Oncology Group
NEA Baptist Clinic
Arkansas Otolaryngology
Hot Springs Radiology
Northwest Arkansas
Center
Services
Pathology
Arkansas Pediatric Clinic
Jacksonville Medical Care
OrthoArkansas
Autumn Road Family Practice
Johnson Dermatology
Ozark Orthopaedics
Arkansas Urology
Little Rock Family Practice
Premier Dermatology
Bowen Hefley Rhodes Stewart Little Rock Pediatric Clinic
Radiology Associates PA
Orthopedics
Magnolia Regional Medical
The Surgical Clinic of Central
CARTI
Center
Arkansas
Conway OBGYN Clinic, PA
MANA Physicians
Southern Regional Anesthesia
Community Physician’s Group
UAMS
Interested in your group joining this list?
Contact Laura Haywood at [email protected] or
501-224-8967 for all the details.
www.ArkMed.org