The Fox Focus Fall/Winter 2015 | Page 2

THE FOX FOCUS... ON RESEARCH by claire meunier I SAM OGDEN “ think it’s really simple. If we don’t do it, it can’t get done. If people with Parkinson’s disease don’t step up, they can’t go from pre-clinical models to a cure,” says Bob Harmon on why he participates in clinical research. Harmon, a Florida resident diagnosed in 2006, volunteers for traditional, in-person studies and says he sees the need for that approach, but he’s also embraced the new wave of technology-enabled virtual studies. “It’s very simple to do; it’s low impact,” he says. The Parkinson’s disease (PD) community, eager for opportunities to advance research by leveraging the latest technology, has keenly welcomed Fox Insight, MJFF’s virtual clinical study launched in March. The study is designed so that patients report symptoms online, building a data set to enhance understanding of the lived experience of Parkinson’s. Researchers aim to identify 2 THE FOX FOCUS patterns or changes in disease over time and among subtypes of PD (e.g., genetic, young-onset) to drive research priorities and design. It will also compare data to a control group without PD. In its first few months, nearly 3,000 individuals — both with and without PD — have enrolled and have completed a total of 3,732 study visits collectively. Data collected through Fox Insight is de-identified and will be made available to the research community starting in early 2016. Study leaders say Fox Insight data will help identify unmet needs rated most critical by people with PD. To date, participants have indicated their most bothersome symptoms to be fatigue, stiffness, erectile dysfunction and reduced libido. “Patients are the experts on their disease,” says MJFF CEO, Todd Sherer, PhD. “Fox Insight is a platform for them to share that expertise and to help shape our areas of research focus. Too often study priorities begin with the scientists’ interests. Our ‘patient-centered research’ approach means that patients are not just the end recipient of new treatments but our partners in the conception of these studies.” Interested volunteers can enroll at foxinsight.org where they will complete a “virtual study visit,” consisting of four online questionnaires, on a quarterly basis. New features and surveys build on this core data to enhance the comprehensive view researchers have of the lived PD experience. In May, Fox Insight launched the first of these additions: “Fox Insight Wear.” continued on page 9› THE SHERER REPORT A NOTE FROM OUR CEO “The road to a cure is not a straight line.” Our Foundation exists to pursue a single, exclusive goal: accelerating a cure for Parkinson’s disease (PD). But the road to a cure is not a straight line. It is lined with way stations, unexpected detours and countless make-or-break moments. One example is the leap from laboratory testing to clinical trials in humans. Though thousands of drugs are tested at the lab bench, only a tiny percentage prove safe and effective enough to warrant testing in people. Advancing to clinical trials is a true research milestone. The Michael J. Fox Foundation (MJFF) pushes promising drugs toward that threshold by investing in the most promising early-stage treatments. We seek out studies with great scientific rationale but in need of resources to test that rationale. It’s a high-risk, h